Search Results - "Huntington's disease"

Huntington's disease

Table of Contents: “…Contents: Clinical features of Huntington's Disease -- Basic pathogenic mechanisms and pathology -- Current drug therapies -- New disease modifying therapies -- Neural transplants.…”
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The molecular biology of Huntington's disease

Subjects: “…Huntington's disease. 90221…”
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Huntington's disease and HD-like disorders

Table of Contents: “…Contents: Huntington's disease -- Huntington's disease like disorders -- Chorea -- Anticipation -- Pathobiology of Huntington's disease -- Huntingtin protein misfolding -- Aggregation -- Ubiquitous expression including in peripheral tissues -- Juvenile Huntington's disease/Westphal variant -- Psychiatric, behavioural and cognitive symptomatology -- HD phenocopies -- C9Orf72 and SCA17.…”
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Cell replacement therapy for neurodegenerative diseases

Table of Contents: “…Contents: Parkinson's Disease and therapies available -- Preclinical data supporting cell therapies for Parkinson's -- Clinical data on fetal transplant trials in Parkinson's -- Development of stem cell-derived dopamine neurons -- Huntington's Disease and therapies available -- Preclinical data supporting cell therapies for Huntington's -- Clinical data on fetal transplant trials in Huntington's -- Development of stem cell-derived medium spiny neurons.…”
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RNAi for neurological diseases

Table of Contents: “…Contents: Repeat expansion diseases -- Polyglutamine (polyQ) repeat diseases -- Huntington's disease -- Vectors for delivering genetic material to brain -- AAVs for delivering RNAi for reducing gene expression -- Artificial miRNAs -- Testing miHD for efficacy -- Off-target silencing -- MRI-guided delivery of AAV into primates -- HTT suppression -- Other gain-of function diseases -- Targeted infusion for broad coverage -- Silencing ataxin-1 -- Nonallele specific silencing: experimental design -- Expression and activity of miSCA1.…”
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Series (RNA interference)
Series (Gene transfer and gene therapy)