Search Results - "Stem Cells."
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Suggested Topics within your search.
- Gene therapy 5
- Genetic Therapy
- Medical genetics 5
- Treatment
- genetics 5
- methods 5
- therapy 5
- Adenoviridae 3
- Adenoviruses 3
- Brain Diseases 3
- Diseases 3
- Gene Transfer Techniques 3
- Genetic Vectors 3
- Genetic transformation 3
- Genetic vectors 3
- Helper Viruses 3
- Hemophilia B 3
- Liver 3
- Liver Diseases 3
- Lung Diseases 3
- Lungs 3
- Ornithine Carbamoyltransferase Deficiency 3
- Therapeutic use 3
- therapeutic use 3
- Animal models in research 2
- CRISPR (Genetics) 2
- CRISPR-Cas Systems 2
- Clustered Regularly Interspaced Short Palindromic Repeats 2
- Duchenne muscular dystrophy 2
- Dystrophin 2
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1
CRISPR editing therapy for Duchenne Muscular Dystrophy part 1 of 2 /
Published 2022Table of Contents: “…Contents: Duchene Muscular Dystrophy (DMD) -- Dystrophin function -- MDX mouse model -- AAV CRISPR local therapy in mice -- AAV CRISPR systemic therapy in mice -- Myogenic stem cells can be transduced and edited by AAV9 CRISPR therapy.…”
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Series
Electronic Video -
2
CRISPR editing therapy for Duchenne Muscular Dystrophy part 1 of 2 /
Published 2022Table of Contents: “…Contents: Duchene Muscular Dystrophy (DMD) -- Dystrophin function -- MDX mouse model -- AAV CRISPR local therapy in mice -- AAV CRISPR systemic therapy in mice -- Myogenic stem cells can be transduced and edited by AAV9 CRISPR therapy.…”
Get full text
Series
Electronic Video -
3
Helper-dependent adenoviral vectors for gene therapy
Published 2014Table of Contents: “…Contents: Overview of gene therapy vectors -- Helper-Dependent Ad (HDAd) vector -- Liver and lung directed gene therapy -- Hemophilia B gene therapy -- OTC deficiency clinical trial -- Balloon occlusion catheter-based delivery of HDAd -- HDAd-mediated CF gene therapy -- Brain gene therapy -- HDAd as genetic vaccine -- HDAd and stem cells.…”
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Series
Electronic Video -
4
Helper-dependent adenoviral vectors for gene therapy
Published 2014Table of Contents: “…Contents: Overview of gene therapy vectors -- Helper-Dependent Ad (HDAd) vector -- Liver and lung directed gene therapy -- Hemophilia B gene therapy -- OTC deficiency clinical trial -- Balloon occlusion catheter-based delivery of HDAd -- HDAd-mediated CF gene therapy -- Brain gene therapy -- HDAd as genetic vaccine -- HDAd and stem cells.…”
Get full text
Series
Electronic Video -
5
Helper-dependent adenoviral vectors for gene therapy
Published 2014Table of Contents: “…Contents: Overview of gene therapy vectors -- Helper-Dependent Ad (HDAd) vector -- Liver and lung directed gene therapy -- Hemophilia B gene therapy -- OTC deficiency clinical trial -- Balloon occlusion catheter-based delivery of HDAd -- HDAd-mediated CF gene therapy -- Brain gene therapy -- HDAd as genetic vaccine -- HDAd and stem cells.…”
Get full text
Series
Electronic Video