Search Results - "Huntington's disease"
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- Diseases 1
- Gene Transfer Techniques 1
- Gene therapy 1
- Genetic Therapy 1
- Genetic Vectors 1
- Genetic aspects 1
- Genetic vectors 1
- Huntington Disease 1
- Huntington's disease 1
- MicroRNAs 1
- Nervous System Diseases 1
- Nervous system 1
- RNA Interference 1
- RNA, Small Interfering 1
- Small interfering RNA 1
- Therapeutic use 1
- methods 1
- therapeutic use 1
- therapy 1
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RNAi for neurological diseases
Published 2014Table of Contents: “…Contents: Repeat expansion diseases -- Polyglutamine (polyQ) repeat diseases -- Huntington's disease -- Vectors for delivering genetic material to brain -- AAVs for delivering RNAi for reducing gene expression -- Artificial miRNAs -- Testing miHD for efficacy -- Off-target silencing -- MRI-guided delivery of AAV into primates -- HTT suppression -- Other gain-of function diseases -- Targeted infusion for broad coverage -- Silencing ataxin-1 -- Nonallele specific silencing: experimental design -- Expression and activity of miSCA1.…”
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Series (RNA interference)
Series (Gene transfer and gene therapy)
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